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13 Publications listed
Personalized CRISPR therapies could soon reach thousands — here’s how
Published 2026
Blood,
Brain,
Eye,
Genomics,
Delivery
University of California, Berkeley - IGI
10.1038/d41586-026-01243-y
Nature . 2026 Apr;652(8111):857-859. doi: 10.1038/d41586-026-01243-y
Protocol: Design and Validation of Mirtron-Mediated RNA Interference for Gene Therapy
Published 2026
Eye
University of Oxford
DOI: 10.1007/978-1-0716-5198-8_14
Methods Mol Biol . 2026:3023:195-206. doi: 10.1007/978-1-0716-5198-8_14.
Genome-scale functional mapping of the mammalian whole brain with in vivo Perturb-seq
Published 2026
Brain
University of Oxford
https://doi.org/10.64898/2026.03.16.711480. Preprint.
bioRxiv [Preprint]. 2026 Mar 18:2026.03.16.711480. doi: 10.64898/2026.03.16.711480.
Exploratory Project Report: Individualised therapies and platform technologies: exploring methodological challenges for NICE project report
Published 2025
University of Oxford
Bias in HD-ISS staging introduced by the FreeSurfer cross-sectional stream: Insights from the Huntington's Disease Young Adult Study (HD-YAS)
Published 2025
Huntington's disease (HD)
Brain
HTT
University College London
DOI: 10.1177/18796397251366900. Epub 2025 Aug 13.
Citation: J Huntingtons Dis. 2025 Nov;14(4):396-402.