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Personalized CRISPR therapies could soon reach thousands — here’s how
Authors: Fyodor D Urnov, Sadik H Kassim
Protocol: Design and Validation of Mirtron-Mediated RNA Interference for Gene Therapy
Protocol: Design and Validation of Mirtron-Mediated RNA Interference for Gene Therapy
Qingyun Zheng, Harry O Orlans, Federica Staurenghi, Michelle E McClements, Robert E MacLaren
Genome-scale functional mapping of the mammalian whole brain with in vivo Perturb-seq
Genome-scale functional mapping of the mammalian whole brain with in vivo Perturb-seq
Tuo Shi, Maria Korshunova, Seoyeon Kim, David DeTomaso, Xinhe Zheng, Lavanya Vishvanath, Thokozile Nyasulu, Nhan Huynh, Alexander Sun, Patrick C Thompson, Yifan Zhang, Emilie M Wigdor, Narjes Rohani, Salma Ali, Huixian Qiu, Michael Geralt, Ziyan Zhao, Sara Rabhi, Zizhen Yao, Cindy Tj van Velthoven, Joseph R Nery, Rosa Gomez Castanon, Severin Dicks, Tiffany J Chen, Joseph R Ecker, Hongkui Zeng, Grace Xy Zheng, Stephan J Sanders, Laksshman Sundaram, Xin Jin